Alexion Pharmaceuticals

09/02/2026

Back to school season often features excitement, and sometimes challenges. Some teens may be navigating hurdles their peers can't see.

At just 13 years old, Nick was diagnosed with generalised (gMG), a rare neurological disease. gMG is characterised by reduced muscle function and severe weakness. For Nick, this sometimes meant his legs giving out and giving excuses as to why he was falling.

Years later, Nick reflects on trying to hide his symptoms because he didn't want to draw extra attention to himself, and how much it meant to have the support of his friends and family.

08/30/2026

Swollen arms and legs, extreme shortness of breath and an abnormal heartbeat can all be signs and symptoms of light chain (AL) , a rare, systemic and progressive disease that involves the buildup of amyloid fibrils in tissues and organs, particularly the heart and kidneys.

Because signs and symptoms can mimic other diseases, it can take up to 3 years to receive a correct diagnosis.

Greater awareness of AL amyloidosis can help support earlier recognition and shorten the path to diagnosis.

Learn more ⬇️

08/18/2026

The barriers are real. The gaps in diagnosis, treatment and support aren't just statistics — they're lived experiences that demand action.

Changing what it means to live with a rare disease isn't something any one of us can do alone. It's something we pioneer together with patients, caregivers, researchers, advocates and communities united by a shared belief: that rare should never mean forgotten.



Swipe to learn why it matters. 👉

08/17/2026

Do you know a nonprofit organization working to improve the rare disease diagnostic journey? The last day to submit an application to the Alexion Charitable Foundation 2026 Grant Cycle is Aug. 21.

Learn more https://alexion.com/alexion-charitable-foundation

The Alexion Charitable Foundation and Alexion, AstraZeneca Rare Disease, are separate legal entities with distinct governance and decision-making protocols and procedures.

The Alexion Charitable Foundation (ACF) is designed to have the most positive impact possible on the communities we serve. Our mission is to address the health disparities within and among the rare disease community. We invest in projects to ensure that all underserved communities – including BIPO...

08/17/2026

Taking the stairs. Reaching into a kitchen cabinet. Daily activities that most people don’t think twice about can be difficult, even painful for those living with (HPP) and may require their careful consideration.

HPP may not always be visible, but its broad range of symptoms, including bone fractures, muscle weakness and fatigue, can be ever-present and affect how one navigates their daily life.

Learn more about how HPP can show itself in daily life below:

08/11/2026

The early symptoms of generalised (gMG) can be easy to mistake for another cause, and because symptoms often fluctuate day to day, doctors may not get the full picture from a single exam.

It might take months or even years to receive a diagnosis, which can have an extended negative impact on quality-of-life.

As a progressive disease, gMG can also lead to more severe symptoms, including difficulty swallowing or even respiratory failure.

Know the signs and symptoms of gMG.

08/10/2026

For many people living with a rare disease, the path to diagnosis can take years. The Alexion Charitable Foundation (ACF) is committed to changing that.

Through its 2026 Grant Cycle, ACF is seeking nonprofit partners who are advancing the rare disease diagnostic journey.

If your organization, or one you know is doing this work, applications are now open: https://alexion.com/alexion-charitable-foundation

The Alexion Charitable Foundation and Alexion, AstraZeneca Rare Disease, are separate legal entities with distinct governance and decision-making protocols and procedures.

The Alexion Charitable Foundation (ACF) is designed to have the most positive impact possible on the communities we serve. Our mission is to address the health disparities within and among the rare disease community. We invest in projects to ensure that all underserved communities – including BIPO...

08/03/2026

The Alexion Charitable Foundation (ACF) has opened its 2026 Grant Cycle.

This year, ACF is placing a deeper focus on improving the rare disease diagnostic journey, seeking proposals in:

🔬 Science-Driven Solutions
💡 Technology & Innovation
🤝 Patient Supports
📋 Research & Policy

Learn more about eligibility and how to apply: https://bit.ly/3RKagjU

The Alexion Charitable Foundation and Alexion, AstraZeneca Rare Disease, are separate legal entities with distinct governance and decision-making protocols and procedures.

The Alexion Charitable Foundation (ACF) is designed to have the most positive impact possible on the communities we serve. Our mission is to address the health disparities within and among the rare disease community. We invest in projects to ensure that all underserved communities – including BIPO...

07/28/2026

The immune system’s job is to protect you.

But in paroxysmal nocturnal haemoglobinuria ( ) red blood cells are missing protective proteins, leaving them exposed to the complement system, a part of the immune system designed to attack threats like infections.

As a result, red blood cell destruction within blood vessels occurs, which increases the risk of serious complications like blood clots.

It’s important to understand how PNH impacts the body to properly manage this rare, chronic, progressive and potentially life-threatening blood disorder.