Neurogene Inc.

Name: Neurogene Inc.
Address: 535 W 24th Street, 5th Floor, New York, NY, 10011, US
Telephone: +18772375020
Price range: Not applicable

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Neurogene Inc.

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Neurogene’s mission is to turn devastating neurological diseases into treatable conditions. For more information, visit www.neurogene.com. laws and regulations.

About Neurogene

The mission of Neurogene is to turn devastating neurological diseases into treatable conditions to improve the lives of patients and families impacted by these rare diseases. Neurogene is developing novel approaches and treatments to address the limitations of conventional gene therapy in central nervous system disorders. This includes selecting a delivery approach to maximize distribution to target tissues and by designing products to maximize potency and purity for an optimized efficacy and safety profile. The company’s novel and proprietary EXACT gene regulation platform technology allows for the delivery of therapeutic levels while limiting transgene toxicity associated with conventional gene therapy. Terms of Use & Community Rules
We think social media is a great way to share what excites us and what we are working on. We look forward to engaging with families and friends of the rare disease community and invite you to be an active participant in the conversation. As a biotechnology company, we operate in a highly regulated industry and are required to adhere to certain laws and regulations. Therefore, all comments submitted to our page must be monitored and reviewed and may be subject to removal. To help ensure that your comments will be taken into consideration and posted, please adhere to the following community rules. We do not allow:
•Offensive, defamatory or obscene language;
•Any reference to pharmaceutical products, treatments or questions related to medical advice;
•Information to pitch products or services; or
•Any adverse events or side effects possibly due to a medication. Any adverse event concerns should be reported immediately to http://www.fda.gov/medwatch or by calling 1-800-FDA-1088. Comments must clearly relate to Neurogene Inc.’s discussion topics. Any posts or comments submitted become the property of Neurogene Inc. and can be removed at our discretion. This page is intended for U.S. residents only, 18 years of age or older, and is governed by U.S. All comments shared are not necessarily reflective of Neurogene Inc. We reserve the right to update our community rules or remove this page, or any of its content or comments, at any time. Any information provided here is for informational purposes and is not a substitute for medical advice from a healthcare professional. Always visit or speak to a qualified healthcare professional regarding your medical condition. All decisions regarding patient care must be handled by a healthcare professional and be made based on the unique needs of each patient. While Neurogene Inc. makes reasonable efforts to include accurate and up-to-date information on this site, Neurogene Inc. makes no representations or warranties as to the accuracy and assumes no liability for any errors or omissions in the content of this site. Read more concerning our Privacy Policy and Terms of Use on our website: https://www.neurogene.com.

10/27/2026

Because is caused by a spontaneous pathogenic variant—or mutation—in a gene called MECP2 that is located on the X chromosome, it can impact anyone. This Rett Syndrome Awareness Month, get to by visiting the International Rett Syndrome Foundation: https://www.rettsyndrome.org/about-rett-syndrome/

10/22/2026

Did you know? Males can also develop . Long-standing assumptions about Rett, as a condition that primarily affects females, have contributed to delayed or missed diagnoses for males. This October, in honor of Rett Syndrome Awareness Month, learn more about Rett syndrome from the International Rett Syndrome Foundation: https://www.rettsyndrome.org/about-rett-syndrome/

10/15/2026

Did you know? can affect all aspects of life. Parents of children with Rett may begin to notice their child miss developmental milestones and lose abilities they had already gained. This Rett Syndrome Awareness Month, we are helping spread by sharing information about this progressive neurodevelopmental disorder to help people get to .

Learn more: https://www.rettsyndrome.org/get-involved/raise-awareness/

10/07/2026

We were honored to attend the St. Louis Strollathon this past weekend, where we met with so many amazing families in the Rett community. Thank you to the International Rett Syndrome Foundation for making it such a fantastic event, and to Canine Companions for being there with their volunteer puppy trainer and service dog in training.

We’re looking forward to the next Strollathons – see if there's one near you: https://www.rettsyndrome.org/get-involved/strollathons/

10/01/2026

October is Rett Syndrome Awareness Month, and we are proud to help raise awareness and foster understanding of alongside the families impacted by Rett. We’re pleased to join the International Rett Syndrome Foundation in sharing information about Rett and celebrating the people of the Rett community.

Learn more: https://www.rettsyndrome.org/about-rett-syndrome/

09/25/2026

This fall, Neurogene is proud to be a sponsor of the International Rett Syndrome Foundation’s Strollathons. Taking place in 11 states across the country, these family-friendly events provide a meaningful way to connect with other families and raise awareness of . Take a look to see if there’s a Strollathon near you: https://www.rettsyndrome.org/get-involved/strollathons/ -a-Strollathon

09/23/2026

Did you know that males can have Rett syndrome too? Last weekend, Neurogene was proud to sponsor and attend the Rett Fest Upstate New York. This inspiring event is organized by the recently established Barrett D. Otis Charitable Fund, which focuses on funding Rett Syndrome research for boys with Rett syndrome. Learn more at: www.bdofund.com

09/22/2026

Thank you to IRSF and to every family who joined Neurogene and the International Rett Syndrome Foundation on September 9th for our Neurogene Community Update webinar. We truly appreciate the opportunity to share information and answer your questions. For more information about some of the topics we discussed, please visit https://www.neurogene.com/patients-and-families . If you missed the webinar, you can watch it at https://youtu.be/oectVknuMFw

Watch the September 9, 2026 edition of Rett in Focus: Neurogene Com...

08/27/2026

At Neurogene, we strive to not just listen to families in the rare disease community, but to truly integrate their perspectives into the core of our work. That’s why we are excited to announce the formation of our new Caregiver Advisory Council – a group of six parents from the community. We are truly grateful to each of them for agreeing to participate and share their insights as parents of sons and daughters ranging from 5 to 29 years old. We look forward to their involvement as we shape our future to align with the needs of families across the community.

08/24/2026

We are looking forward to meeting with the Rett syndrome community on Wednesday, September 9th at 12 p.m. ET, and we hope you’ll join us! Thank you to the International Rett Syndrome Foundation for hosting and providing the opportunity to share updates. Zoom registration link available below.

Registration is now open for the next Rett in Focus webinar!

Join IRSF on Wednesday, September 9th, at 12 p.m. ET for Rett in Focus: Neurogene Community Update, featuring information from Neurogene Inc. about NGN-401, its investigational gene therapy for Rett syndrome.

Building on updates shared at the ASCEND 2026 National Summit, Neurogene will discuss recent developments in the NGN-401 clinical program and what they anticipate will come next. Families can also hear about new educational resources and community initiatives, including Neurogene Cares and its Caregiver Advisory Council.

The webinar will include a moderated Q&A based on questions submitted in advance during registration.

Register: https://us02web.zoom.us/webinar/register/WN_-Qxmq0ksSZugZHt_iMK5BQ

Address

535 W 24th Street, 5th Floor
New York, NY
10011

Telephone

+18772375020

Website

http://www.neurogene.com/, https://www.linkedin.com/company/neurogeneinc/

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